- 15-10-2020Developing Digital Endpoints For the Gaucher Community
- 15-10-2020AVAILABLE TO WATCH NOW: AAV-Based Gene Therapy and Prevail Therapeutic's Approach For Neuronopathic Gaucher Diseases & Parkinson's Disease with a GBA Mutation
- 13-10-2020Encouraging the Voice of the Patient In a New Trial Looking At In Utero Treatment For NGD At University of California San Francisco
- 05-10-2020AVAILABLE TO WATCH NOW: Ex Vivo Gene Therapy For Type 1 Gaucher Disease
- 05-10-2020AVAILABLE TO WATCH NOW: IGD Home Therapy Webinar
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The IGA is organizing an event for young adult Gaucher patients giving them a unique opportunity to exchange information and ideas.
Gaucher Disease is an autosomal recessive disease and the most common Lysosomal Storage Disorder. It is caused by deficiency of a specific enzyme in the body, caused by a genetic mutation received from both parents.
International Gaucher Day 'Rare But Not Alone' is celebrated annually on 1 October. Find out more information about how to get involved by clicking here.
Humanitarian Aid has always been a priority for the IGA; we have always pledged to help any Gaucher patient who asks us for help wherever they live in the world.
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