To mark Rare Disease Day 2021, we are pleased to publish our new information booklet on Gaucher disease Types 1, 2 and 3: DOWNLOAD THE BOOKLET HERE
We have developed this booklet as a source of information for patients and their carers and to …
As many countries are still in lockdown, people including those living with Gaucher disease are spending a lot of time at home. The IGA is supporting its members in these difficult times with a webinar: ‘Wellness for …
PR001 in development by Prevail Therapeutics
Prevail Therapeutics, a wholly-owned subsidiary of Eli Lilly and Company, is developing an investigational gene therapy called PR001 that has the potential to slow or stop the underlying …