- 15-01-2020AVROBIO Announces Clinical and Regulatory Progress For Gaucher Disease Program
- 10-01-2020PR001 Administered to International Type 2 Gaucher Disease Patient Via Compassionate Use Pathway
- 08-01-2020Prevail Therapeutics Is Recruiting Patients For PROPEL, a Clinical Trial Testing An Investigational Gene Therapy Called PR001 to Treat Parkinson’s Disease In People with GBA Mutations
- 17-12-2019December 2019 Newsletter
- 12-12-2019IGA's Membership Grows to 55 Member Associations From 54 Countries
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The IGA is organizing an event for young adult Gaucher patients giving them a unique opportunity to exchange information and ideas.
Gaucher Disease is an autosomal recessive disease and the most common Lysosomal Storage Disorder. It is caused by deficiency of a specific enzyme in the body, caused by a genetic mutation received from both parents.
International Gaucher Day 'Rare But Not Alone' is celebrated annually on 1 October. Find out more information about how to get involved by clicking here.
Humanitarian Aid has always been a priority for the IGA; we have always pledged to help any Gaucher patient who asks us for help wherever they live in the world.
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